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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
Duchenne DMD dystrophy
Long noncoding RNA
CaVβs
Animal/physiopathology
Inbred mdx
Multi resolution modeling
Metabolism
Knockout
Duchenne muscular dystrophy DMD
Dystrophie Musculaire de Becker BMD
Cell Line
Dystrophy
Energy Metabolism/drug effects
Muscle
Myotendinous junction
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Human Umbilical Vein Endothelial Cells
Molecular Sequence Data
Inhibitors
MES
Dystrophine
Myogenesis
Becker muscular dystrophy BMD
Calcium
Autophagy
Activin Receptors
CaV subunits
Muscle development
Muscles/physiopathology
Muscle Strength
Male
Epigenetics
Cardiomyopathie
Skeletal muscle
Molecular docking
Modificateurs de gènes
Homeostasis
Dynamin 2
NAD+
Gene Expression Regulation/drug effects
MiARN
Mdx mouse
Génomique
Muscular dystrophy
Duchenne muscular dystrophy
Invivo
Gene expression
Cells
Centronuclear myopathy
Muscle Biology
Delivery
NNOS
Muscular Dystrophy
CD38
LKB1
Calcium Channels
L-Type
Inbred C57BL
Mitochondrial fission
DMO
BMD
Cell homeostasis
DMD
Dystrophin
Long QT
Hear
Becker muscular dystrophy
Diseases
Clinical trials
Multi exon skipping
Cell Biology
Genomic
Exon skipping
Cardiomyopathy
Dystrophin-EGFP
Allele‐specific silencing therapy
Morphogenesis
Cachexia
LncARN
DHPR α1S
Muscular Atrophy
Ex-vivo
Liver
Base Sequence
Drp1
Dystrophin central domain
Hepatocellular carcinoma
Gene modifiers
LncRNA
Dystrophie musculaire de Becker
Humans
CTNNB1
Mice
Multiresolution modeling
Becker BMD muscular dystrophy
Dystrophie Musculaire de Duchenne DMD
Animals
Antisense oligonucleotides
Immunoglobulin Fc Fragments/pharmacology
Cultured